Efficient production of human FVIII in hemophilic mice using lentiviral vectors (Q45861949)

17 December 2017

title

Efficient production of human FVIII in hemophilic mice using lentiviral vectors (English)

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17 December 2017

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Neeltje A Kootstra

1

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17 December 2017

Ryusuke Matsumura

series ordinal

2

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17 December 2017

Inder M Verma

series ordinal

3

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17 December 2017

publication date

1 May 2003

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17 December 2017

published in

Molecular Therapy

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17 December 2017

volume

7

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17 December 2017

issue

5 Pt 1

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17 December 2017

page(s)

623-631

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17 December 2017

The molecular basis of hemophilia A in man.

cites work

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

Distribution of factor VIII mRNA and antigen in human liver and other tissues

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

Detection of factor VIII/coagulant antigen in human liver tissue

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

Ultrastructural localization of factor VIII procoagulant antigen in human liver hepatocytes

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

Toward gene therapy for hemophilia A: long-term persistence of factor VIII-secreting fibroblasts after transplantation into immunodeficient mice.

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

In vivo production of human factor VII in mice after intrasplenic implantation of primary fibroblasts transfected by receptor-mediated, adenovirus-augmented gene delivery

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

Gene therapy for hemophilia A: production of therapeutic levels of human factor VIII in vivo in mice

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

Long-term persistence of human bone marrow stromal cells transduced with factor VIII-retroviral vectors and transient production of therapeutic levels of human factor VIII in nonmyeloablated immunodeficient mice

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

Genetic induction of immune tolerance to human clotting factor VIII in a mouse model for hemophilia A

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

Vesicular stomatitis virus G glycoprotein pseudotyped retroviral vectors: concentration to very high titer and efficient gene transfer into mammalian and nonmammalian cells

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

Long-term expression of human coagulation factor VIII and correction of hemophilia A after in vivo retroviral gene transfer in factor VIII-deficient mice

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

Short-term correction of factor VIII deficiency in a murine model of hemophilia A after delivery of adenovirus murine factor VIII in utero

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

Partial correction of murine hemophilia A with neo-antigenic murine factor VIII.

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

Systemic delivery of an adenoviral vector encoding canine factor VIII results in short-term phenotypic correction, inhibitor development, and biphasic liver toxicity in hemophilia A dogs.

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

Coexpression of factor VIII heavy and light chain adeno-associated viral vectors produces biologically active protein

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

Development of a self-inactivating lentivirus vector.

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

In vivo gene delivery and stable transduction of nondividing cells by a lentiviral vector

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

Gene transfer by lentiviral vectors is limited by nuclear translocation and rescued by HIV-1 pol sequences

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

Expression vector system based on the chicken beta-actin promoter directs efficient production of interleukin-5.

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

Efficient selection for high-expression transfectants with a novel eukaryotic vector

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

HIV-1 genome nuclear import is mediated by a central DNA flap

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

Woodchuck hepatitis virus contains a tripartite posttranscriptional regulatory element.

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

Targeted disruption of the mouse factor VIII gene produces a model of haemophilia A

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

Sustained expression of genes delivered directly into liver and muscle by lentiviral vectors

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

Transduction of human CD34+ cells that mediate long-term engraftment of NOD/SCID mice by HIV vectors

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

Transduction of liver cells by lentiviral vectors: analysis in living animals by fluorescence imaging.

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

Efficient gene delivery and targeted expression to hepatocytes in vivo by improved lentiviral vectors

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

Induction of tolerance to human factor VIII in mice

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

Use of a liver-specific promoter reduces immune response to the transgene in adenoviral vectors

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

Lentiviral vectors containing the human immunodeficiency virus type-1 central polypurine tract can efficiently transduce nondividing hepatocytes and antigen-presenting cells in vivo

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

Stable transduction of quiescent CD34(+)CD38(-) human hematopoietic cells by HIV-1-based lentiviral vectors

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

In vitro selection of lentivirus vector-transduced human CD34+ cells

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

A third-generation lentivirus vector with a conditional packaging system

1 reference

https://api.crossref.org/works/10.1016%2FS1525-0016%2803%2900073-X

7 January 2021

10.1016/S1525-0016(03)00073-X

Identifiers

DOI

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17 December 2017

1 reference

17 December 2017