Delivery of full-length factor VIII using a piggyBac transposon vector to correct a mouse model of hemophilia A. (Q35225590)

7 August 2017

title

Delivery of full-length factor VIII using a piggyBac transposon vector to correct a mouse model of hemophilia A. (English)

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7 August 2017

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Coagulation factor VIII

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6

Shinya Yamanaka

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7 August 2017

Akitsu Hotta

8

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Noriko Sasakawa

3

object named as

Noriko Sasakawa

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7 August 2017

2

Naoko Fujimoto

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7 August 2017

Hideto Matsui

1

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7 August 2017

Yasuhide Ohinata

4

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7 August 2017

Midori Shima

5

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7 August 2017

Mitsuhiko Sugimoto

7

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7 August 2017

language of work or name

English

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publication date

15 August 2014

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7 August 2017

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7 August 2017

volume

9

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7 August 2017

issue

8

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7 August 2017

page(s)

e104957

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Creative Commons Attribution 4.0 International

7 August 2017

copyright license

start time

15 August 2014

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April 2022 Public Data File from Crossref

copyright status

copyrighted

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cites work

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A novel cell-sheet technology that achieves durable factor VIII delivery in a mouse model of hemophilia A

27 July 2018

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Adenovirus-associated virus vector-mediated gene transfer in hemophilia B

27 July 2018

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Nanotechnology for therapy and imaging of liver diseases

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A microRNA-regulated and GP64-pseudotyped lentiviral vector mediates stable expression of FVIII in a murine model of Hemophilia A.

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Neonatal helper-dependent adenoviral vector gene therapy mediates correction of hemophilia A and tolerance to human factor VIII

27 July 2018

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Gene transfer efficiency and genome-wide integration profiling of Sleeping Beauty, Tol2, and piggyBac transposons in human primary T cells

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27 July 2018

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Complete correction of hemophilia A with adeno-associated viral vectors containing a full-size expression cassette

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Persistent expression of factor VIII in vivo following nonprimate lentiviral gene transfer

27 July 2018

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27 July 2018

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27 July 2018

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27 July 2018

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27 July 2018

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Long-term expression of human coagulation factor VIII in a tolerant mouse model using the φC31 integrase system.

27 July 2018

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Hyperactive piggyBac gene transfer in human cells and in vivo.

26 September 2018

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In vivo genome editing restores haemostasis in a mouse model of haemophilia

26 September 2018

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Gene therapy strategies for hemophilia: benefits versus risks

26 September 2018

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26 September 2018

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26 September 2018

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26 September 2018

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Ex vivo gene therapy for hemophilia A that enhances safe delivery and sustained in vivo factor VIII expression from lentivirally engineered endothelial progenitors

26 September 2018

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26 September 2018

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26 September 2018

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Multiyear therapeutic benefit of AAV serotypes 2, 6, and 8 delivering factor VIII to hemophilia A mice and dogs

26 September 2018

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Phenotypic correction and long-term expression of factor VIII in hemophilic mice by immunotolerization and nonviral gene transfer using the Sleeping Beauty transposon system

26 September 2018

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https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4134236

A complementary transposon tool kit for Drosophila melanogaster using P and piggyBac

26 September 2018

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https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4134236

Total correction of hemophilia A mice with canine FVIII using an AAV 8 serotype.

26 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4134236

Efficient production of human FVIII in hemophilic mice using lentiviral vectors

26 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4134236

Acute direct adenoviral vector cytotoxicity and chronic, but not acute, inflammatory responses correlate with decreased vector-mediated transgene expression in the brain

26 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4134236

Hydrodynamics-based transfection in animals by systemic administration of plasmid DNA.

26 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4134236

Abnormal factor VIII Hiroshima: defect in crucial proteolytic cleavage by thrombin at Arg1689 detected by a novel ELISA.

26 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4134236

Novel forms of B-domain-deleted recombinant factor VIII molecules. Construction and biochemical characterization

26 September 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/25126862

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

A fresh look at iPS cells

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/25126862

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Identifiers

DOI

10.1371/JOURNAL.PONE.0104957

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7 August 2017

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1 reference

7 August 2017

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