Bodywide skipping of exons 45-55 in dystrophic mdx52 mice by systemic antisense delivery (Q36187202)

12 August 2017

Bodywide skipping of exons 45-55 in dystrophic mdx52 mice by systemic antisense delivery (English)

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12 August 2017

7

Stephanie M R Duguez

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12 August 2017

8

Kanneboyina Nagaraju

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12 August 2017

9

Eric P Hoffman

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12 August 2017

Yoshitsugu Aoki

1

1 reference

12 August 2017

Toshifumi Yokota

2

1 reference

12 August 2017

Tetsuya Nagata

3

1 reference

12 August 2017

Akinori Nakamura

4

1 reference

12 August 2017

Jun Tanihata

5

1 reference

12 August 2017

Takashi Saito

6

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12 August 2017

Terence Partridge

10

1 reference

12 August 2017

Shin'ichi Takeda

11

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12 August 2017

language of work or name

English

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publication date

6 August 2012

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12 August 2017

6

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Proceedings of the National Academy of Sciences of the United States of America

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published in

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12 August 2017

109

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12 August 2017

34

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12 August 2017

13763-13768

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describes a project that uses

12 August 2017

ImageJ

1 reference

11 June 2022

https://www.ebi.ac.uk/europepmc/webservices/rest/PMC3427064/fullTextXML

inferred from PubMed Central ID database lookup

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Dystrophin quantification and clinical correlations in Becker muscular dystrophy: implications for clinical trials

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Exon skipping and dystrophin restoration in patients with Duchenne muscular dystrophy after systemic phosphorodiamidate morpholino oligomer treatment: an open-label, phase 2, dose-escalation study

1 October 2017

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Restoring dystrophin expression in duchenne muscular dystrophy muscle progress in exon skipping and stop codon read through

1 October 2017

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Systemic administration of PRO051 in Duchenne's muscular dystrophy

1 October 2017

1 reference

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In-frame Dystrophin Following Exon 51-Skipping Improves Muscle Pathology and Function in the Exon 52–Deficient mdx Mouse

1 October 2017

1 reference

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Antisense PMO found in dystrophic dog model was effective in cells from exon 7-deleted DMD patient

1 October 2017

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1 October 2017

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Vivo-Morpholinos: a non-peptide transporter delivers Morpholinos into a wide array of mouse tissues

1 October 2017

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Dystrophins carrying spectrin-like repeats 16 and 17 anchor nNOS to the sarcolemma and enhance exercise performance in a mouse model of muscular dystrophy.

1 October 2017

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Theoretic applicability of antisense-mediated exon skipping for Duchenne muscular dystrophy mutations

1 October 2017

1 reference

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A renaissance for antisense oligonucleotide drugs in neurology: exon skipping breaks new ground

1 October 2017

1 reference

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Assessment of the feasibility of exon 45-55 multiexon skipping for Duchenne muscular dystrophy

1 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3427064

Optimizing exon skipping therapies for DMD.

1 October 2017

1 reference

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IDT SciTools: a suite for analysis and design of nucleic acid oligomers

1 October 2017

1 reference

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Follow-up of three patients with a large in-frame deletion of exons 45-55 in the Duchenne muscular dystrophy (DMD) gene

1 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3427064

Antisense-induced exon skipping for duplications in Duchenne muscular dystrophy

1 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3427064

Systemic delivery of antisense oligoribonucleotide restores dystrophin expression in body-wide skeletal muscles

1 October 2017

1 reference

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ESEfinder: A web resource to identify exonic splicing enhancers

1 October 2017

1 reference

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alpha1-syntrophin gene disruption results in the absence of neuronal-type nitric-oxide synthase at the sarcolemma but does not induce muscle degeneration

1 October 2017

1 reference

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Morpholino antisense oligomers: design, preparation, and properties

1 October 2017

1 reference

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Dystrophin: the protein product of the Duchenne muscular dystrophy locus

1 October 2017

1 reference

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The molecular basis for Duchenne versus Becker muscular dystrophy: correlation of severity with type of deletion

1 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3427064

Myogenic cell lines derived from transgenic mice carrying a thermolabile T antigen: a model system for the derivation of tissue-specific and mutation-specific cell lines

1 October 2017

1 reference

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The Pathology of Paralysis with Muscular Degeneration (Paralysie Myosclerotique), or Paralysis with Apparent Hypertrophy

2 July 2018

1 reference

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Efficacy of systemic morpholino exon-skipping in Duchenne dystrophy dogs

23 September 2018

1 reference

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Asymptomatic Becker muscular dystrophy in a family with a multiexon deletion

23 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3427064

Antisense oligonucleotide-induced exon skipping restores dystrophin expression in vitro in a canine model of DMD.

23 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3427064

Targeted Disruption of Exon 52 in the Mouse Dystrophin Gene Induced Muscle Degeneration Similar to That Observed in Duchenne Muscular Dystrophy

23 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3427064

Exon-skipping therapy for Duchenne muscular dystrophy

23 September 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/22869723

12 December 2020

inferred from PubMed ID database lookup

Multiexon skipping leading to an artificial DMD protein lacking amino acids from exons 45 through 55 could rescue up to 63% of patients with Duchenne muscular dystrophy

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/22869723

12 December 2020

inferred from PubMed ID database lookup

Identifiers

DOI

10.1073/PNAS.1204638109

1 reference

12 August 2017

0 references

1 reference

12 August 2017

PubMed publication ID

22869723

1 reference