(Q51143641)

31 March 2018

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:17164775%20AND%20SRC:MED&resulttype=core&format=json

30 May 2020

title

Phenotypic Correction of α-Sarcoglycan Deficiency by Intra-arterial Injection of a Muscle-specific Serotype 1 rAAV Vector (English)

1 reference

31 March 2018

Phenotypic correction of alpha-sarcoglycan deficiency by intra-arterial injection of a muscle-specific serotype 1 rAAV vector (English)

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:17164775%20AND%20SRC:MED&resulttype=core&format=json

30 May 2020

2

Marc Bartoli

2 references

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:17164775%20AND%20SRC:MED&resulttype=core&format=json

30 May 2020

31 March 2018

author name string

Francoise Fougerousse

1

2 references

31 March 2018

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:17164775%20AND%20SRC:MED&resulttype=core&format=json

30 May 2020

Jérôme Poupiot

3

2 references

31 March 2018

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:17164775%20AND%20SRC:MED&resulttype=core&format=json

30 May 2020

Ludovic Arandel

4

2 references

31 March 2018

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:17164775%20AND%20SRC:MED&resulttype=core&format=json

30 May 2020

Muriel Durand

5

2 references

31 March 2018

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:17164775%20AND%20SRC:MED&resulttype=core&format=json

30 May 2020

Nicolas Guerchet

6

2 references

31 March 2018

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:17164775%20AND%20SRC:MED&resulttype=core&format=json

30 May 2020

Evelyne Gicquel

7

2 references

31 March 2018

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:17164775%20AND%20SRC:MED&resulttype=core&format=json

30 May 2020

Olivier Danos

8

2 references

31 March 2018

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:17164775%20AND%20SRC:MED&resulttype=core&format=json

30 May 2020

Isabelle Richard

9

2 references

31 March 2018

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:17164775%20AND%20SRC:MED&resulttype=core&format=json

30 May 2020

publication date

1 January 2007

2 references

31 March 2018

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:17164775%20AND%20SRC:MED&resulttype=core&format=json

30 May 2020

2 references

31 March 2018

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:17164775%20AND%20SRC:MED&resulttype=core&format=json

30 May 2020

volume

15

2 references

31 March 2018

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:17164775%20AND%20SRC:MED&resulttype=core&format=json

30 May 2020

issue

1

2 references

31 March 2018

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:17164775%20AND%20SRC:MED&resulttype=core&format=json

30 May 2020

page(s)

53-61

2 references

31 March 2018

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:17164775%20AND%20SRC:MED&resulttype=core&format=json

Primary adhalinopathy (alpha-sarcoglycanopathy): clinical, pathologic, and genetic correlation in 20 patients with autosomal recessive muscular dystrophy.

30 May 2020

cites work

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300022

7 January 2021

Therapy insight: cardiovascular complications associated with muscular dystrophies

1 reference

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7 January 2021

Missense mutations in the adhalin gene linked to autosomal recessive muscular dystrophy

1 reference

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7 January 2021

Deficiency of a glycoprotein component of the dystrophin complex in dystrophic muscle

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7 January 2021

Molecular and cell biology of the sarcoglycan complex

1 reference

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7 January 2021

Filamin 2 (FLN2): A muscle-specific sarcoglycan interacting protein

1 reference

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7 January 2021

Bidirectional Signaling between Sarcoglycans and the Integrin Adhesion System in Cultured L6 Myocytes

1 reference

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7 January 2021

Progressive muscular dystrophy in alpha-sarcoglycan-deficient mice

1 reference

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7 January 2021

Sarcoglycan isoforms in skeletal muscle

1 reference

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7 January 2021

Muscles of mice deficient in alpha-sarcoglycan maintain large masses and near control force values throughout the life span

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300022

7 January 2021

Early adenovirus-mediated gene transfer effectively prevents muscular dystrophy in alpha-sarcoglycan-deficient mice

1 reference

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7 January 2021

Delivery of alpha- and beta-sarcoglycan by recombinant adeno-associated virus: efficient rescue of muscle, but differential toxicity

1 reference

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7 January 2021

Noninvasive monitoring of therapeutic gene transfer in animal models of muscular dystrophies.

1 reference

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7 January 2021

Femoral intra-arterial injection: a tool to deliver and assess recombinant AAV constructs in rodents whole hind limb

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300022

7 January 2021

Rescue of skeletal muscles of gamma-sarcoglycan-deficient mice with adeno-associated virus-mediated gene transfer.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300022

7 January 2021

Expression of the primary coxsackie and adenovirus receptor is downregulated during skeletal muscle maturation and limits the efficacy of adenovirus-mediated gene delivery to muscle cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300022

7 January 2021

Functional Rescue of the Sarcoglycan Complex in the BIO 14.6 Hamster Using δ-Sarcoglycan Gene Transfer

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300022

7 January 2021

Muscle-specific promoters may be necessary for adeno-associated virus-mediated gene transfer in the treatment of muscular dystrophies.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300022

7 January 2021

Full functional rescue of a complete muscle (TA) in dystrophic hamsters by adeno-associated virus vector-directed gene therapy

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300022

7 January 2021

rAAV vector-mediated sarcogylcan gene transfer in a hamster model for limb girdle muscular dystrophy

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300022

7 January 2021

Stable restoration of the sarcoglycan complex in dystrophic muscle perfused with histamine and a recombinant adeno-associated viral vector

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300022

7 January 2021

Safety and efficacy of AAV-mediated calpain 3 gene transfer in a mouse model of limb-girdle muscular dystrophy type 2A.

1 reference

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7 January 2021

Regional intravascular delivery of AAV-2-F.IX to skeletal muscle achieves long-term correction of hemophilia B in a large animal model

1 reference

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7 January 2021

Long-term pharmacologically regulated expression of erythropoietin in primates following AAV-mediated gene transfer.

1 reference

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7 January 2021

Repeated adeno-associated virus serotype 2 aerosol-mediated cystic fibrosis transmembrane regulator gene transfer to the lungs of patients with cystic fibrosis: a multicenter, double-blind, placebo-controlled trial

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300022

7 January 2021

AAV-mediated factor IX gene transfer to skeletal muscle in patients with severe hemophilia B.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300022

7 January 2021

Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300022

7 January 2021

Gene therapy strategies for Duchenne muscular dystrophy utilizing recombinant adeno-associated virus vectors.

1 reference

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7 January 2021

Synthetic muscle promoters: activities exceeding naturally occurring regulatory sequences

1 reference

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7 January 2021

Transduction and utility of the granulocyte-macrophage colony-stimulating factor gene into monocytes and dendritic cells by adeno-associated virus.

1 reference

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7 January 2021

Further observations on the pathological responses of rat skeletal muscle to toxins isolated from the venom of the Australian tiger snake, Notechis scutatus scutatus

1 reference

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7 January 2021

Persistent and therapeutic concentrations of human factor IX in mice after hepatic gene transfer of recombinant AAV vectors

1 reference

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7 January 2021

MUSEAP, a novel reporter gene for the study of long-term gene expression in immunocompetent mice

1 reference

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7 January 2021

Novel approach to quantitative polymerase chain reaction using real-time detection: application to the detection of gene amplification in breast cancer

1 reference

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7 January 2021

Force impairment in calpain 3-deficient mice is not correlated with mechanical disruption.

1 reference

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7 January 2021

A noninvasive procedure to detect muscle weakness in the mdx mouse

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7 January 2021

Identifiers

DOI

10.1038/SJ.MT.6300022

2 references

31 March 2018

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:17164775%20AND%20SRC:MED&resulttype=core&format=json

30 May 2020

1 reference

31 March 2018

reason for deprecated rank

incorrect identifier value

0 references

1 reference